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Title | VALENS: A Ph 1/2, Random'd, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate Safety/Preliminary Efficacy of AT342, an AAV8-Delivered Gene Transfer Therapy in Crigler-Najjar Syndrome Subjects Aged 1 Yr and Older |
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Disease/Condition | Heart and Vascular Diseases,Brain and Neurological,Gastroenterology & Liver Diseases,Pediatrics,Crigler-Najjar Syndrome,Metabolic Diseases |
Eligibility Criteria | Click here for eligibility requirements |
Principal Investigator | Nadia Ovchinsky, MD |
Contact Name | Sharon Thomas |
Contact Email | sharotho@montefiore.org |
IRB/Protocol Number | 2017-7918 |
Status | Active/Enrolling |
Adult Clinical Trial | Yes |
Pediatric Clinical Trial | Yes |
Sub-Specialty | Gastroenterology - Liver |