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Title | A Phase 2b/3 Prospective, Randomized, Double-Blind, Sham-Controlled Trial of VTS-270 (2-hydroxypropyl---cyclodextrin) in Subjects with Neurologic Manifestations of Niemann-Pick Type C1 (NPC1) Disease |
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Disease/Condition | Genetics |
Eligibility Criteria | Click here for eligibility requirements |
Principal Investigator | Paul Levy |
Contact Name | Jessica Fischetti |
Contact Email | jfischet@montefiore.org |
IRB/Protocol Number | IRB# 16-10-18-01 |
Status | Enrolling |
Adult Clinical Trial | No |
Pediatric Clinical Trial | No |